Patent · US Active

Nucleic acids and methods for the treatment of Pompe disease

US10059947B2 · kind B2 · utility

2Cited by
2References
22Claims
0Family size

Assignee

Inventors

Key dates

Filing dateSep 10, 2014
Grant dateAug 28, 2018
Priority date—
Expiry dateSep 10, 2034

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2320/33
  • WIPO fieldBiotechnology
  • WIPO sectorChemistry

Abstract

The invention relates to nucleic acids and methods for restoring acid alpha-glucosidase (GAA) activity in patients with Pompe disease using splice-switching technology.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.