Compound and method for treating myotonic dystrophy
US10106796B2 · kind B2 · utility
1Cited by
10References
16Claims
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Key dates
| Filing date | Aug 20, 2014 |
| Grant date | Oct 23, 2018 |
| Priority date | — |
| Expiry date | Aug 20, 2034 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2810/40
- WIPO fieldBiotechnology
- WIPO sectorChemistry
Abstract
Provided are 9-base morpholino antisense compounds targeted to polyCUG repeats in the 3′UTR region of dystrophia myotonica protein kinase (DMPK) mRNA, and related methods for treating myotonic dystrophy DM1.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.