Patent · US Active

Methods of treating Mucopolysaccharidosis IIIB (MPSIIIB)

US10413597B2 · kind B2 · utility

0Cited by
11References
10Claims
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Inventors

Key dates

Filing dateSep 29, 2015
Grant dateSep 17, 2019
Priority date
Expiry dateNov 9, 2035

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12Y302/0105
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Methods for treating the central nervous system (CNS) in a human patient with mucopolysaccharidosis (MPS) MB who has an intact blood brain barrier, comprising intravenous administration of recombinant NaGlu.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.