Methods and compounds useful in conditions related to repeat expansion
US10435430B2 · kind B2 · utility
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44References
17Claims
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Key dates
| Filing date | Jul 31, 2014 |
| Grant date | Oct 8, 2019 |
| Priority date | — |
| Expiry date | Jul 31, 2034 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2320/34
- WIPO fieldOrganic fine chemistry
- WIPO sectorChemistry
Abstract
Described are compounds and methods useful for the treatment and investigation of diseases and disorders associated with expanded repeat-containing RNA molecules. In certain embodiments, compounds and methods useful for the modulation of ATXN-3 pre-mRNA are described. In certain embodiments, compounds and methods useful for the modulation of ATN-1 mRNA are described.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.