Patent · US Active

Compositions and methods for diagnosis and treatment of neuromuscular disorders

US10603296B1 · kind B1 · utility

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1References
9Claims
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Assignee

Inventors

Key dates

Filing dateApr 8, 2019
Grant dateMar 31, 2020
Priority date
Expiry dateApr 8, 2039

Classification

  • Technology area (CPC A)Human Necessities
  • CPC primaryA61K31/417
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Compositions including small molecule biochemicals, and salts and derivatives thereof, and methods for detection, treatment or prophylaxis of neuromuscular disorders are provided, including modulation of microRNA that contribute to neuromuscular disorders, including muscular dystrophies, peripheral motor neuron diseases, motor neuron diseases, neuromuscular junction diseases, myopathies, metabolic diseases of the muscle, amyotrophic lateral sclerosis, multiple sclerosis, Parkinson's disease, motor neuron diseases, Huntington's disease, spinocerebellar ataxia, and spinal muscular atrophy.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.