Compositions and methods for diagnosis and treatment of neuromuscular disorders
US10603296B1 · kind B1 · utility
Assignee
Inventors
Key dates
| Filing date | Apr 8, 2019 |
| Grant date | Mar 31, 2020 |
| Priority date | — |
| Expiry date | Apr 8, 2039 |
Classification
- Technology area (CPC A)Human Necessities
- CPC primaryA61K31/417
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Compositions including small molecule biochemicals, and salts and derivatives thereof, and methods for detection, treatment or prophylaxis of neuromuscular disorders are provided, including modulation of microRNA that contribute to neuromuscular disorders, including muscular dystrophies, peripheral motor neuron diseases, motor neuron diseases, neuromuscular junction diseases, myopathies, metabolic diseases of the muscle, amyotrophic lateral sclerosis, multiple sclerosis, Parkinson's disease, motor neuron diseases, Huntington's disease, spinocerebellar ataxia, and spinal muscular atrophy.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.