Therapeutic targeting of a microRNA to treat Duchenne muscular dystrophy
US10626395B2 · kind B2 · utility
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24Claims
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Key dates
| Filing date | Sep 18, 2017 |
| Grant date | Apr 21, 2020 |
| Priority date | — |
| Expiry date | Sep 18, 2037 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2320/35
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Methods of treating Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD), comprising administering an inhibitory nucleic acid that targets miR-128.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.