Patent · US Active

Chemical molecules that inhibit the slicing mechanism for treating diseases resulting from splicing anomalies

US10654813B2 · kind B2 · utility

0Cited by
14References
2Claims
0Family size

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Key dates

Filing dateOct 5, 2018
Grant dateMay 19, 2020
Priority date
Expiry dateOct 5, 2038

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC07D401/14
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Compounds and pharmaceutically acceptable salts thereof that may be used to treat a disease, for example, Duchenne muscular dystrophy, AIDS, and progeria. The compounds and pharmaceutically acceptable salts thereof may be part of a pharmaceutical composition including a pharmaceutically acceptable support.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.