Patent · US Active

Modified polynucleotides for the production of secreted proteins

US10703789B2 · kind B2 · utility

34Cited by
33References
14Claims
0Family size

Assignee

Inventors

Key dates

Filing dateJun 12, 2019
Grant dateJul 7, 2020
Priority date
Expiry dateJun 12, 2039

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2840/00
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

A pharmaceutical composition which has a plurality of lipid nanoparticles that has a mean particle size of between 80 nm and 160 nm and contains a modified mRNA encoding a polypeptide. The lipid nanoparticles include a cationic lipid, a neutral lipid, a cholesterol, and a PEG lipid. The mRNA contains a 5′-cap, 5′-UTR, N1-methyl-pseudouridine, a 3′-UTR, and a poly-A region with at least 100 nucleotides.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.