Gene therapy vectors for treatment of Danon disease
US10703797B2 · kind B2 · utility
1Cited by
3References
15Claims
0Family size
Assignee
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Key dates
| Filing date | Dec 27, 2019 |
| Grant date | Jul 7, 2020 |
| Priority date | — |
| Expiry date | Dec 27, 2039 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2830/008
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The disclosure relates to optimized polynucleotide sequences for LAMP-2B, expression cassettes, vectors, and methods of use thereof in treating disease, e.g. Danon disease.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.