Modified factor IX, and compositions, methods and uses for gene transfer to cells, organs, and tissues
US10799566B2 · kind B2 · utility
5Cited by
8References
64Claims
0Family size
Assignee
Inventors
Key dates
| Filing date | Jun 23, 2016 |
| Grant date | Oct 13, 2020 |
| Priority date | — |
| Expiry date | Jun 23, 2036 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2750/14143
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The invention relates to modified Factor IX coding sequence, expression cassette, vectors such as viral (e.g., lenti- or adeno-associated viral) vectors, and gene transfer methods and uses. In particular, to target Factor IX nucleic acid to cells, tissues or organs for expression (transcription) of Factor IX.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.