Genome-modified recombinant adeno-associated virus vectors
US10900053B2 · kind B2 · utility
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30Claims
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Key dates
| Filing date | Nov 21, 2015 |
| Grant date | Jan 26, 2021 |
| Priority date | — |
| Expiry date | Jan 23, 2036 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2830/002
- WIPO fieldBiotechnology
- WIPO sectorChemistry
Abstract
Provided herein are recombinant adeno-associated virus (rAAV) nucleic acid vectors that comprise one or more modifications within at least one inverted terminal repeat (ITR) region. Exemplary modifications include ITR sequences comprising a glucocorticoid responsive element and/or a transcription factor binding site. Also provided are plasmids, libraries, rAAV particles, compositions, kits, and methods related to such vectors.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.