Methods and compositions for genome engineering
US10968261B2 · kind B2 · utility
2Cited by
50References
12Claims
0Family size
Assignee
Inventors
Key dates
| Filing date | Aug 21, 2018 |
| Grant date | Apr 6, 2021 |
| Priority date | — |
| Expiry date | Nov 16, 2038 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2750/14143
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Disclosed herein are methods and compositions for insertion of transgene sequences encoding proteins that is aberrantly expressed in disease or disorder such as a lysosomal storage disease.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.