Patent · US Active

Nucleic acid-polypeptide compositions and methods of inducing exon skipping

US10994020B2 · kind B2 · utility

25Cited by
78References
24Claims
0Family size

Assignee

Inventors

Key dates

Filing dateSep 11, 2018
Grant dateMay 4, 2021
Priority date
Expiry dateSep 11, 2038

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2320/33
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Disclosed herein are molecules and pharmaceutical compositions that induce an insertion, deletion, duplication, or alteration in an incorrectly spliced mRNA transcript to induce exon skipping or exon inclusion. Also described herein include methods for treating a disease or disorder that comprises a molecule or a pharmaceutical composition that induces an insertion, deletion, duplication, or alteration in an incorrectly spliced mRNA transcript to induce exon skipping or exon inclusion.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.