Methods and compositions for modulating splicing
US11091475B2 · kind B2 · utility
1Cited by
65References
13Claims
0Family size
Assignee
Inventors
Key dates
| Filing date | Mar 13, 2020 |
| Grant date | Aug 17, 2021 |
| Priority date | — |
| Expiry date | Mar 13, 2040 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2310/333
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Described herein are small molecule splicing modulator compounds that modulate splicing of mRNA, such as pre-mRNA, encoded by genes, and methods of use of the small molecule splicing modulator compounds for modulating splicing and treating diseases and conditions.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.