Nucleic acids and methods for the treatment of Pompe disease
US11104903B2 · kind B2 · utility
1Cited by
3References
18Claims
0Family size
Assignee
Inventors
Key dates
| Filing date | Jul 23, 2018 |
| Grant date | Aug 31, 2021 |
| Priority date | — |
| Expiry date | Jul 23, 2038 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2320/33
- WIPO fieldBiotechnology
- WIPO sectorChemistry
Abstract
The invention relates to nucleic acids and methods for restoring acid alpha-glucosidase (GAA) activity in patients with Pompe disease using splice-switching technology.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.