Patent · US Active

Frataxin expression constructs

US11116852B2 · kind B2 · utility

1Cited by
8References
23Claims
0Family size

Assignee

Inventors

Key dates

Filing dateNov 8, 2017
Grant dateSep 14, 2021
Priority date
Expiry dateJul 27, 2038

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2830/002
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

The invention provides polynucleotides, vectors and viruses expressing frataxin and methods of treating Friedreich's Ataxia.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.