Patent · US Active

Methods for modulating splicing

US11129829B2 · kind B2 · utility

3Cited by
18References
19Claims
0Family size

Assignee

Inventors

Key dates

Filing dateMar 9, 2020
Grant dateSep 28, 2021
Priority date
Expiry dateMar 9, 2040

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N15/63
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Described herein are methods of use of small molecule splicing modulator compounds that modulate splicing of mRNA, such as pre-mRNA, encoded by genes, and methods of treating diseases and conditions associated with gene expression or activity of proteins encoded by genes.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.