Method for enhancing folding and transport of misfolded glucocerebrosidase
US11160773B2 · kind B2 · utility
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22Claims
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Key dates
| Filing date | Apr 20, 2020 |
| Grant date | Nov 2, 2021 |
| Priority date | — |
| Expiry date | Apr 20, 2040 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12Y302/01045
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Therapeutic compositions and methods for treatment of late-onset Gaucher disease are described herein. The compositions comprise compounds having activity as pharmacological chaperones for mutant forms of the beta-glucocerebrosidase. Methods of treatment involve providing therapeutically effective amounts of such compositions to subjects in need thereof.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.