Patent · US Active

Methods and compositions for modulating splicing

US11162101B2 · kind B2 · utility

1Cited by
66References
17Claims
0Family size

Assignee

Inventors

Key dates

Filing dateFeb 4, 2020
Grant dateNov 2, 2021
Priority date
Expiry dateFeb 4, 2040

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2310/333
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Described herein are small molecule splicing modulator compounds that modulate splicing of mRNA, such as pre-mRNA, encoded by genes, and methods of use of the small molecule splicing modulator compounds for modulating splicing and treating diseases and conditions.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.