Patent · US Active

Nucleic acid-polypeptide compositions and methods of inducing exon skipping

US11179472B2 · kind B2 · utility

28Cited by
78References
25Claims
0Family size

Assignee

Inventors

Key dates

Filing dateSep 12, 2018
Grant dateNov 23, 2021
Priority date
Expiry dateSep 12, 2038

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2320/33
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Disclosed herein are molecules and pharmaceutical compositions that induce an insertion, deletion, duplication, or alteration in an incorrectly spliced mRNA transcript to induce exon skipping or exon inclusion. Also described herein include methods for treating a disease or disorder that comprises a molecule or a pharmaceutical composition that induces an insertion, deletion, duplication, or alteration in an incorrectly spliced mRNA transcript to induce exon skipping or exon inclusion.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.