Codon optimized GLA genes and uses thereof
US11198858B2 · kind B2 · utility
1Cited by
3References
23Claims
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Key dates
| Filing date | Apr 26, 2021 |
| Grant date | Dec 14, 2021 |
| Priority date | — |
| Expiry date | Apr 26, 2041 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2840/00
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The present disclosure provides codon optimized nucleotide sequences encoding human alpha-galactosidase A, vectors, and host cells comprising codon optimized alpha-galactosidase A sequences, and methods of treating disorders such as Fabry disease comprising administering to the subject a codon optimized sequence encoding human alpha-galactosidase A.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.