Gene therapy for treating mucopolysaccharidosis type II
US11253612B2 · kind B2 · utility
1Cited by
53References
24Claims
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Key dates
| Filing date | Apr 14, 2017 |
| Grant date | Feb 22, 2022 |
| Priority date | — |
| Expiry date | Nov 3, 2038 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2830/15
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
A suspension useful for AAV9-mediated intrathecal and/or systemic delivery of an expression cassette containing a hIDS gene is provided herein. Also provided are methods and kits containing these vectors and compositions useful for treating Hunter syndrome and the symptoms associated with Hunter syndrome.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.