Patent · US Active

Materials and methods for treatment of primary hyperoxaluria type 1 (PH1) and other alanine-glyoxylate aminotransferase (AGXT) gene related conditions or disorders

US11407997B2 · kind B2 · utility

0Cited by
140References
15Claims
0Family size

Assignee

Inventors

Key dates

Filing dateFeb 21, 2018
Grant dateAug 9, 2022
Priority date
Expiry dateOct 16, 2038

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2310/20
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

The present application provides materials and methods for treating a patient with one or more conditions or disorders associated with AGXT, both ex vivo or in vivo. For example, the present disclosure provides materials and methods for treating a patient with Primary Hyperoxaluria Type 1 (PH1). The present application also provides materials and methods for editing an AGXT gene in a cell by genome editing. The present application also provides materials and methods for altering a contiguous genomic sequence of an AGXT gene in a cell. In addition, the present application provides one or more gRNAs for editing an AGXT gene. The present application also provides a therapeutic comprising at least one or more gRNAs for editing an AGXT gene. In addition, the present application provides a therapeutic for treating a patient with an AGXT related condition or disorder.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.