Materials and methods for treatment of friedreich ataxia and other related disorders
US11564997B2 · kind B2 · utility
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14Claims
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Key dates
| Filing date | Jun 22, 2017 |
| Grant date | Jan 31, 2023 |
| Priority date | — |
| Expiry date | Mar 6, 2039 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2800/80
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The present application provides materials and methods for treating a patient with one or more condition associated with FXN whether ex vivo or in vivo. In addition, the present application provides materials and methods for editing and/or modulating the expression of FXN gene in a cell by genome editing.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.