Patent · US Active

Methods and compositions for modulating splicing

US11603531B1 · kind B1 · utility

0Cited by
66References
22Claims
0Family size

Assignee

Inventors

Key dates

Filing dateOct 15, 2021
Grant dateMar 14, 2023
Priority date
Expiry dateOct 15, 2041

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2310/333
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Described herein are small molecule splicing modulator compounds that modulate splicing of mRNA, such as pre-mRNA, encoded by genes, and methods of use of the small molecule splicing modulator compounds for modulating splicing and treating diseases and conditions.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.