Patent · US Active

Treatment of monogenetic disorders

US11634472B2 · kind B2 · utility

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8Claims

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Assignee

ZENTRUM FÜR FORSCHUNGSFÖRDERUNG IN DER PÄDIATRIE GMBH

Inventors

Helmut Hanenberg · Düsseldorf, DE
Maj-Kristin Holz · Essen, DE
Katharina Röllecke · Dortmund, DE
Katharina Waack-Buchholz · Essen, DE

Key dates

Filing date	Feb 21, 2018
Grant date	Apr 25, 2023
Priority date	—
Expiry date	Jul 27, 2039

Classification

Technology area (CPC C)Chemistry; Metallurgy
CPC primaryC12N2830/46
WIPO fieldPharmaceuticals
WIPO sectorChemistry

Abstract

The present invention relates to a nucleic acid expression cassette, in particular for the expression of a human liver-specific and/or liver-expressed protein and/or preferably physiologically active domains and/or fragments thereof in a patient suffering from a monogenetic disorder caused by a mutation in the gene coding for the liver-specific and/or liver-expressed protein.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.