Patent · US Active

Adeno-associated viral vectors for treatment of Niemann-Pick Disease type-C

US11905523B2 · kind B2 · utility

0Cited by

122References

20Claims

0Family size

Assignee

Ginkgo Bioworks, Inc. · US

Inventors

Daniel McCoy · Durham, US
Garrett E. Berry · Durham, US
David Dismuke · Cary, US

Key dates

Filing date	Oct 16, 2020
Grant date	Feb 20, 2024
Priority date	—
Expiry date	Dec 17, 2041

Classification

Technology area (CPC C)Chemistry; Metallurgy
CPC primaryC12N2830/50
WIPO fieldPharmaceuticals
WIPO sectorChemistry

Abstract

Provided herein are gene therapy compositions and methods for treating, preventing, and/or curing NPC1. More specifically, the disclosure provides Adeno-associated virus (AAV) vectors for delivery of nucleic acids and nucleic acids (including AAV transfer cassettes) for treating, preventing, and/or curing NPC1.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.