Allele-specific silencing therapy for dynamin 2-related diseases
US11926829B2 · kind B2 · utility
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9Claims
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Key dates
| Filing date | Feb 3, 2021 |
| Grant date | Mar 12, 2024 |
| Priority date | — |
| Expiry date | Oct 10, 2041 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12Y306/05005
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The invention relates to an allele specific siRNA able to silence the expression of only one allele of a heterozygous DNM2 gene, for treating diseases caused by heterozygous mutation and/or overexpression of Dynamin 2.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.