Nucleic acid-polypeptide compositions and methods of inducing exon skipping
US12064483B2 · kind B2 · utility
13Cited by
101References
24Claims
0Family size
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Key dates
| Filing date | Jun 17, 2022 |
| Grant date | Aug 20, 2024 |
| Priority date | — |
| Expiry date | Aug 9, 2042 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2320/33
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Disclosed herein are molecules and pharmaceutical compositions that induce an insertion, deletion, duplication, or alteration in an incorrectly spliced mRNA transcript to induce exon skipping or exon inclusion. Also described herein include methods for treating a disease or disorder that comprises a molecule or a pharmaceutical composition that induces an insertion, deletion, duplication, or alteration in an incorrectly spliced mRNA transcript to induce exon skipping or exon inclusion.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.