Nucleic acids and methods for the treatment of Pompe disease
US12091665B2 · kind B2 · utility
0Cited by
4References
13Claims
0Family size
Assignee
Inventors
Key dates
| Filing date | Aug 3, 2021 |
| Grant date | Sep 17, 2024 |
| Priority date | — |
| Expiry date | Jan 26, 2042 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2320/33
- WIPO fieldBiotechnology
- WIPO sectorChemistry
Abstract
The invention relates to nucleic acids and methods for restoring acid alpha-glucosidase (GAA) activity in patients with Pompe disease using splice-switching technology.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.