Adeno-associated virus compositions for restoring PAH gene function and methods of use thereof
US12203094B2 · kind B2 · utility
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Key dates
| Filing date | Oct 19, 2020 |
| Grant date | Jan 21, 2025 |
| Priority date | — |
| Expiry date | Nov 23, 2043 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2750/14143
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Provided herein are adeno-associated virus (AAV) compositions that can restore phenylalanine hydroxylase (PAH) gene function in cell. Also provided are methods of use of the AAV compositions, and packaging systems for making the AAV compositions.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.