Compositions and methods for treating Pompe disease
US12251430B2 · kind B2 · utility
0Cited by
3References
15Claims
0Family size
Assignee
Inventors
Key dates
| Filing date | Feb 8, 2021 |
| Grant date | Mar 18, 2025 |
| Priority date | — |
| Expiry date | Jul 12, 2042 |
Classification
- Technology area (CPC A)Human Necessities
- CPC primaryA61K2039/55
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The present application provides methods of treating Pompe disease such as infantile-onset Pompe disease (IOPD) using a pharmaceutical composition comprising an oligosaccharide-acid α-glucosidase (GAA) conjugate, such as avalglucosidase alfa. Also provided are formulations of the oligosaccharide-GAA conjugates.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.