CFTR-modulating compositions and methods
US12270029B2 · kind B2 · utility
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15Claims
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Assignee
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Key dates
| Filing date | Sep 20, 2023 |
| Grant date | Apr 8, 2025 |
| Priority date | — |
| Expiry date | Sep 20, 2043 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2740/16043
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The disclosure provides, e.g., compositions, systems, and methods for targeting, editing, modifying, or manipulating a host cell's genome at one or more locations in a DNA sequence in a cell, tissue, or subject. Gene modifying systems for treating cystic fibrosis, e.g., in subjects having a mutation resulting in F508del, are described.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.