Intrathecal delivery of recombinant adeno-associated virus encoding methyl-CpG binding protein 2
US12357663B2 · kind B2 · utility
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Key dates
| Filing date | Jan 2, 2023 |
| Grant date | Jul 15, 2025 |
| Priority date | — |
| Expiry date | Jan 2, 2043 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2750/14143
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
Methods and materials for intrathecal delivery of recombinant Adeno-associated virus 9 (rAAV9) encoding Methyl-CpG binding protein 2 (MECP2) are provided. Use of the methods and materials is contemplated, for example, for the treatment of Rett syndrome.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.