Recombinant adeno-associated viral vectors for treating Bietti Crystalline Dystrophy
US12371474B2 · kind B2 · utility
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Key dates
| Filing date | Jan 11, 2024 |
| Grant date | Jul 29, 2025 |
| Priority date | — |
| Expiry date | Jan 11, 2044 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2830/50
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The present disclosure provides a recombinant adeno-associated vector comprising a codon-optimized sequence encoding CYP4V2 linked to selected gene expression regulatory sequences and its use in treating Bietti Crystalline Dystrophy (BCD).
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.