Substituted pyrrolo [2,3-d]pyrimidines for treating familial dysautonomia
US12398140B2 · kind B2 · utility
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6References
13Claims
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Key dates
| Filing date | Feb 10, 2020 |
| Grant date | Aug 26, 2025 |
| Priority date | — |
| Expiry date | Jun 6, 2042 |
Classification
- Technology area (CPC A)Human Necessities
- CPC primaryA61P25/00
- WIPO fieldOrganic fine chemistry
- WIPO sectorChemistry
Abstract
The present description relates to compounds of formula (I) useful for improving pre-mRNA splicing in a cell. In particular, another aspect described herein relates to substituted pyrrolo[2,3-d]pyrimidine compounds, forms, and pharmaceutical compositions thereof and methods of use for treating or ameliorating familial dysautonomia.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.