Patent · US Expired

Deoxynojirimycin derivatives and their uses as glucosylceramidase inhibitors

US6177447A · kind A · utility

17Cited by
0References
7Claims
0Family size

Assignee

Inventors

Key dates

Filing dateApr 30, 1999
Grant dateJan 23, 2001
Priority date
Expiry dateApr 30, 2019

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC07D211/46
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Deoxynojirimycin derivatives containing a large hydrophobic moiety, such as cholesterol or adamantame-methanol, linked through a spacer, such as pentamethylene, to the nitrogen atom of deoxynojirimycin, and salts thereof, inhibit glucosylceramidase and may be useful in the treatment of diseases involving a ceramide-mediated signaling process, such as Gaucher disease.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.