Methods and compositions for use in gene therapy for treatment of hemophilia
US7998734B2 · kind B2 · utility
12Cited by
9References
8Claims
0Family size
Assignee
Inventors
Key dates
| Filing date | Oct 31, 2007 |
| Grant date | Aug 16, 2011 |
| Priority date | — |
| Expiry date | May 31, 2029 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2750/14151
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The invention includes a composition comprising a recombinant adeno-associated viral vector comprising at least two adeno-associated virus inverted terminal repeats, a promoter/regulatory sequence, isolated DNA encoding Factor IX and accompanying 5′ and 3′ untranslated regions and a transcription termination.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.