Patent · US Active

RAAV-based compositions and methods

US10597656B2 · kind B2 · utility

11Cited by
25References
10Claims
0Family size

Assignee

Inventors

Key dates

Filing dateAug 9, 2018
Grant dateMar 24, 2020
Priority date
Expiry dateAug 9, 2038

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2750/14143
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

The invention relates to isolated nucleic acids and rAAV-based compositions, methods and kits useful for treating genetic diseases (e.g., alpha-1 antitrypsin deficiency).

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.