Patent · US Active

RAAV-based compositions and methods

US11920133B2 · kind B2 · utility

0Cited by
35References
22Claims
0Family size

Assignee

Inventors

Key dates

Filing dateJan 14, 2022
Grant dateMar 5, 2024
Priority date
Expiry dateMay 14, 2042

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2750/14143
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

The invention relates to isolated nucleic acids and rAAV-based compositions, methods and kits useful for treating genetic diseases (e.g., alpha-1 antitrypsin deficiency).

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.