Patent · US Active

Methods and compositions for modulating alpha-1-antitrypsin expression

US9340784B2 · kind B2 · utility

7Cited by
42References
14Claims
0Family size

Assignee

Inventors

Key dates

Filing dateMar 19, 2013
Grant dateMay 17, 2016
Priority date
Expiry dateMar 19, 2033

Classification

  • Technology area (CPC C)Chemistry; Metallurgy
  • CPC primaryC12N2310/346
  • WIPO fieldPharmaceuticals
  • WIPO sectorChemistry

Abstract

Disclosed herein are methods for decreasing AIAT mRNA and protein expression and treating, ameliorating, preventing, slowing progression, or stopping progression of fibrosis. Disclosed herein are methods for decreasing AIAT mRNA and protein expression and treating, ameliorating, preventing, slowing progression, or stopping progression of liver disease, such as, AIATD associated liver disease, and pulmonary disease, such as, AIATD associated pulmonary disease in an individual in need thereof. Methods for inhibiting AIAT mRNA and protein expression can also be used as a prophylactic treatment to prevent individuals at risk for developing a liver disease, such as, AIATD associated liver disease and pulmonary disease, such as, AIATD associated pulmonary disease.

Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.