Gene correction of SCID-related genes in hematopoietic stem and progenitor cells
US9833479B2 · kind B2 · utility
4Cited by
56References
9Claims
0Family size
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Key dates
| Filing date | Mar 14, 2017 |
| Grant date | Dec 5, 2017 |
| Priority date | — |
| Expiry date | Mar 14, 2037 |
Classification
- Technology area (CPC A)Human Necessities
- CPC primaryA61K2035/124
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The present disclosure is in the field of genome engineering, particularly targeted integration of a functional SCID-related genes (e.g., IL2RG, RAG1 and/or RAG2 gene) into the genome of a cell for provision of proteins lacking or deficient in SCID.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.