Globin gene therapy for treating hemoglobinopathies
US11717579B2 · kind B2 · utility
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61Claims
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Key dates
| Filing date | Mar 3, 2017 |
| Grant date | Aug 8, 2023 |
| Priority date | — |
| Expiry date | Dec 5, 2037 |
Classification
- Technology area (CPC C)Chemistry; Metallurgy
- CPC primaryC12N2830/50
- WIPO fieldPharmaceuticals
- WIPO sectorChemistry
Abstract
The presently disclosed subject matter provides for expression cassettes that allow for expression of a globin gene or a functional portion thereof, vectors comprising thereof, and cells transduced with such expression cassettes and vectors. The presently disclosed subject matter further provides methods for treating a hemoglobinopathy in a subject comprising administering an effective amount of such transduced cells to the subject.
Source: USPTO / EPO open patent data. Objective bibliographic and citation counts.